Table 2 Benefit score of the orphan drug benefit assessment processes
| Data analysis | Number of events (n) | Percentage of overall data% | Number of events (n) | Percentage of overall data% |
|---|---|---|---|---|
| Benefit score | Applied | Granted | ||
| Major | 45 | 56% | 10 | 12% |
| Considerable | 21 | 26% | 0 | 0% |
| Minor | 4 | 5% | 20 | 25% |
| Not quantifiable | 11 | 14% | 49 | 60% |
| No additional benefit | – | – | 2 | 2% |
| Comparison | ||||
| Matching benefit scores | 15 | 19% | – | – |